ION337-CS1 - Clinical Trial
Who Can Participate in the Study?
Age Group
Children
Study Details
Full Title
Phase 1-2, Open-Label, Single and Multiple Ascending Dose Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally-Administered ION337 in Patients with Dravet Syndrome
Principal Investigator
Muhammad Zafar, MD
Pediatric Epileptologist
Protocol Number
IRB:
PRO00119824
NCT:
NCT07531745
Phase
Phase I/II
ClinicalTrials.gov
View on ClinicalTrials.gov
Enrollment Status
Open for Enrollment